Functionality of a bicistronic construction containing HEXA and HEXB genes encoding β-hexosaminidase A for cell-mediated therapy of GM2 gangliosidoses

Alisa A. Shaimardanova, Daria S. Chulpanova, Valeriya V. Solovyeva, Aleksandr M. Aimaletdinov, Albert A. Rizvanov

Neural Regeneration Research . 2022, (1): 122 -129 . DOI: 10.4103/1673-5374.314310