利用基因工程骨髓间充质干细胞移植治疗成年和少年亨廷顿氏病的临床试验
Clinical trial perspective for adult and juvenile Huntington’s disease using genetically-engineered mesenchymal stem cells
Peter Deng, Audrey Torrest, Kari Pollock, Heather Dahlenburg, Geralyn Annett, Jan A. Nolta, Kyle D. Fink
中国神经再生研究(英文版) . 2016, (5): 702 -705 .  DOI: 10.4103/1673-5374.182682