GM2神经节苷脂病的治疗:静脉内给予HexA过表达的hUCBMC的可行性
Functionality of a bicistronic construction containing HEXA and HEXB genes encoding β-hexosaminidase A for cell-mediated therapy of GM2 gangliosidoses
Alisa A. Shaimardanova, Daria S. Chulpanova, Valeriya V. Solovyeva, Aleksandr M. Aimaletdinov, Albert A. Rizvanov
中国神经再生研究(英文版) . 2022, (1): 122 -129 .  DOI: 10.4103/1673-5374.314310